Collaborate Disseminate
Developing effective treatments for genetic lung diseases such as cystic fibrosis has proven challenging. That might not be the case for much longer, with scientists developing a new type of nanoparticle that can carry gene-editing technology directly … Continue reading New nanoparticles deliver gene-editing tech directly into the lungs
Nearly six million Americans currently live with Alzheimer’s disease (AD), with the figure set to climb to 13.8 million by 2050. And with promising trials failing close to the finish line, researchers are desperate for any breakthroughs that will lead to halting the devastating neurodegenerative disease.
Tags: Alzheimer’s Disease, Dementia, gene therapy, Brain
Continue reading Calcium-control gene offers new avenue for Alzheimer’s disease therapy
It’s been about seven years since researchers used the CRISPER gene-editing system to reverse a blindness-inducing condition called retinitis pigmentosa in stem cells outside the body. Now, using a more refined version of CRISPR, a different research t… Continue reading Vision restored in mice thanks to refined CRISPR system
Migraine and glucose-related traits such as fasting insulin and type 2 diabetes are widely understood to be common comorbid disorders, but now scientists have a concrete genetic link that could see a new area of therapy developed for the debilitating d… Continue reading Genetic link between migraine and blood sugar levels confirmed
Amyotrophic lateral sclerosis (ALS) is a debilitating neurodegenerative disease with poor outcomes, but a pair of new studies may point towards a more optimistic future. In tests in human cells and live mice, the scientists identified a gene and a prot… Continue reading Scientists discover two new potential avenues of treatment for ALS
Researchers studying the hearts of healthy centenarians have homed in on a specific genetic mutation that seems to play a crucial role in maintaining cardiovascular functions in old age. Across a series of lab and animal experiments the researchers dem… Continue reading Unique gene mutation in superagers could rewind heart age by a decade
Scientists at Harvard Medical School have investigated why we age, and identified a possible way to reverse it. In tests in mice, the team showed that epigenetic “software glitches” drive the symptoms of aging – and a system reboot can reverse them, po… Continue reading Epigenetic “reboot” reverses aging in mice and could extend lifespan
Science is often a piecemeal process, progressing slowly through the incremental accumulation of knowledge. In the world of medical science this is particularly evident as small targeted research findings one year may, or may not, lead to massive life-… Continue reading The biggest medical milestones of 2022
A rare genetic disease that renders children without a functioning immune system from birth has been effectively cured by an experimental gene therapy. A new study is reporting on the first 10 children treated with the therapy, all of whom are now heal… Continue reading Gene therapy cures kids with rare “bubble-boy” disease in new trial
A Phase 3 trial testing the world’s first topical gene therapy has reported extraordinary results in children suffering from a rare blistering skin disease. The gene therapy gel was seen to completely heal wounds that had been open for years.Continue R… Continue reading World-first topical gene therapy gel heals decades-old wounds