Collaborate Disseminate
Vertex and CRISPR Therapeutics have presented new data from one of the first trials testing gene-editing therapy in human subjects. Fifteen months on from the first patient treatment, the highly experimental therapy is showing remarkable efficacy treat… Continue reading More early data revealed from landmark CRISPR gene editing human trial
Part of what makes cancer so deadly is its ability to rapidly spread to other parts of the body, leading doctors into a deadly game of Whack-A-Mole. Now, researchers at Tulane University have identified a pair of genes that helps triple negative breast… Continue reading Blocking genes halts growth, spread of triple negative breast cancer
A compelling new study, led by scientists from Washington University School of Medicine in St. Louis, has found a novel gene therapy can prevent obesity and build muscle without the need for additional exercise, in mice being fed a high-fat diet.Contin… Continue reading Experimental gene therapy prevents obesity, builds muscle, without exercise or dieting
The results of a first human trial testing a gene therapy for complete color blindness have been published in the journal JAMA Ophthalmology. The research suggests the experimental gene therapy is safe, and potentially efficacious, opening the door to … Continue reading Gene therapy for color blindness passes first phase of human testing
The human body is good at replenishing cells to repair damage, but one vital organ lacks this ability – the heart. But now, researchers at the University of Texas Southwestern Medical Center have uncovered a suite of proteins in mice that could be swit… Continue reading Flipping a protein switch could help hearts heal after an attack
Unfortunately for heart attack patients, heart cells don’t naturally replenish, so this vital organ stays permanently damaged. But now, Cambridge researchers have stumbled onto a gene that appears to trigger heart cell regeneration – and they did so by… Continue reading Cancer study stumbles onto potential way to regenerate heart cells
The CRISPR gene-editing tool has been used inside the human body for the first time. In a new clinical trial, scientists at the Oregon Health and Science University (OHSU) are testing the technique as a treatment for a genetic mutation that causes blin… Continue reading First in-body CRISPR human trial targets hereditary blindness
A newly published statement from the US Food & Drug Administration (FDA) has revealed inaccurate, intentionally manipulated data was included as part of a submission for a major new gene therapy that was approved for public use in May. Th… Continue reading Pharma giant admits data manipulation in FDA application for multi-million-dollar gene therapy
The CRISPR gene-editing system is a powerful tool that looks set to revolutionize the way we treat diseases, as well as basically anything else that can benefit from precisely manipulating DNA. The problem is that sometimes cutting and pastin… Continue reading New CRISPR-based system inserts new DNA without cutting and pasting